QLT announces completion of Phase Ia safety trial of its synthetic retinoid product
2009年3月12日 - 8:00PM
PRニュース・ワイアー (英語)
VANCOUVER, March 12 /PRNewswire-FirstCall/ -- QLT Inc. (NASDAQ:
QLTI; TSX: QLT) ("QLT" or the "Company") today announced the
results from a Phase Ia trial of QLT091001 in healthy adult
volunteers. The trial demonstrated the drug is safe and
well-tolerated and achieved its primary goal of estimating an
appropriate dose for studies in patients. QLT091001 is an orally
administered synthetic retinoid replacement for 11-cis-retinal,
which is a key biochemical component of the visual retinoid cycle.
The drug is being developed for the potential treatment of Leber's
Congenital Amaurosis (LCA), an inherited progressive retinal
degenerative disease that leads to retinal dysfunction and visual
impairment beginning at birth. The Phase Ia trial is an open-label,
single center, ascending dose trial conducted by QLT to evaluate
the safety and tolerance of multiple administrations of the
synthetic retinoid drug in 20 healthy adult volunteers.
Participants were enrolled in 6 cohorts of increasing doses.
Patients in the highest dose cohort reported mild adverse events
(including facial flushing and headache) which were transient in
nature and were resolved during the treatment period. These are
expected adverse events in the retinoid class. No serious adverse
events related to the study treatment were reported. "We are
pleased to report that QLT091001 demonstrated an adequate safety
profile in healthy adults," said Bob Butchofsky, President and
Chief Executive Officer of QLT. "Our next step is to speak with the
Canadian health authorities to determine future clinical
development plans. We expect to initiate a Phase Ib trial in the
second half of 2009 in pediatric patients with LCA, a disease which
affects one in one hundred thousand newborns world-wide for which
there are currently no available treatments." About Synthetic
Retinoid Drugs Genetic diseases in the eye such as LCA and
Retinitis Pigmentosa (RP) arise from gene mutations of enzymes or
proteins required in the biochemistry of vision. QLT091001 is a
replacement for 11-cis-retinal which is an essential component of
the retinoid-rhodopsin cycle and visual function. Two different
gene mutations (Retinal pigment epithelium protein 65 (RPE65) and
lecithin-retinol acyltransferase (LRAT) result in an inadequate
production of 11-cis-retinal and occur in approximately 10% of
patients with LCA and to a lesser extent in RP. The basis for using
synthetic retinoids as replacement therapy for conditions where
genetic defects result in deficiency of 11-cis-retinal is founded
on experiments in mouse genetic models. These experiments used mice
that have mutations in either the RPE65 or LRAT genes, the same as
those associated with LCA in humans. Both mouse models have
clinical features of the human disease. The biological activity of
the synthetic retinoid was monitored by measuring the level of
pigment-related compounds in the eye. Retinal function was also
assessed by detecting electroretinograms (ERGs) and electrical
nerve signals from the retina. Oral administration of QLT091001
showed evidence of having corrected the biochemical defect in the
retinoid cycle in light-sensing cells (rods) and appeared to
restore ERG responses to light in both models of LCA. About Leber's
Congenital Amaurosis LCA is an inherited degenerative retinal
disease characterized by abnormalities such as roving eye movements
and sensitivity to light, and manifesting in severe vision loss
from birth. Eye examinations of infants with LCA reveal normal
appearing retinas. However, low level of retinal activity, measured
by electroretinography, indicates very little visual function.
About QLT QLT Inc. is a global biopharmaceutical company dedicated
to the discovery, development and commercialization of innovative
therapies. Our research and development efforts are focused on
pharmaceutical products in the field of ophthalmology. In addition,
we utilize three unique technology platforms, photodynamic therapy,
Atrigel(R) and punctal plugs with drugs, to create products such as
Visudyne(R) and Eligard(R), and future product opportunities. For
more information, visit our web site at http://www.qltinc.com/. In
April of 2006, QLT entered into an exclusive worldwide
co-development and licensing agreement with Retinagenix, LLC to
develop active synthetic retinoid products for the treatment of
degenerative retinal diseases. Pre-clinical studies have
demonstrated that orally administered synthetic retinoid drugs
cause long-lasting restoration of retinal function. Under the terms
of the agreement, QLT is responsible for developing and
commercializing the products for use in ocular and all other human
diseases. Retinagenix has participated in research in support of
the co-development collaboration and is eligible to receive
payments upon achievement of certain development, approval and
sales milestones as well as a royalty on net sales. QLT Plug
Delivery, Inc. is a wholly-owned subsidiary of QLT Inc. Atrigel is
a registered trademark of QLT USA, Inc. Visudyne is a registered
trademark of Novartis AG. Eligard is a registered trademark of
Sanofi-aventis. QLT Inc. is listed on The NASDAQ Stock Market under
the trading symbol "QLTI" and on The Toronto Stock Exchange under
the trading symbol "QLT." Certain statements contained in this
press release, which are not historical facts, are "forward-looking
statements," of QLT within the meaning of the Private Securities
Litigation Reform Act of 1995 and constitute "forward-looking
information" within the meaning of applicable Canadian securities
laws. Such statements include, but are not limited to: our beliefs
regarding the potential benefits, targets, market opportunity and
commercial success of our synthetic retinoid drug; our expectations
regarding our clinical development plans and strategy for the
technology and timelines associated with these; and statements
which contain language such as "expects," "will," "plans,"
"estimates," "intends," "believes" and similar expressions that do
not relate to historical matters. Forward-looking statements are
predictions only which involve known and unknown risks,
uncertainties and other factors that may cause our actual results
to be materially different from the results expressed or implied by
such statements. Many such risks, uncertainties and other factors
are taken into account as part of our assumptions underlying these
forward-looking statements and include, among others, the
following: risks and uncertainties associated with the timing,
expense and outcome of research and development programs and
commercialization of products (including the difficulty of
predicting the timing and outcome of the synthetic retinoid drug
development efforts, clinical testing and regulatory approvals or
actions); uncertainties regarding the impact of competitive
products and pricing; risks and uncertainties associated with the
safety and effectiveness of our technology; risks and uncertainties
related to the scope, validity, and enforceability of our
intellectual property rights and the impact of patents and other
intellectual property of third parties; and other factors as
described in detail in QLT's Annual Report on Form 10-K, Quarterly
Reports on Form 10-Q and other filings with the U.S. Securities and
Exchange Commission and Canadian securities regulatory authorities.
Forward-looking statements are based on the current expectations of
QLT and QLT does not assume any obligation to update such
information to reflect later events or developments except as
required by law. DATASOURCE: QLT Inc. CONTACT: QLT Inc. Media
Contact: Vancouver, Canada, Karen Peterson, Telephone: (604)
707-7000 or 1-800-663-5486, Fax: (604) 707-7001; The Trout Group
Investor Relations Contact: New York, USA, Christine Yang,
Telephone: (646) 378-2929; or Marcy Strickler, Telephone: (646)
378-2927
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